Turning genes into medicines—what have we learned from gene therapy drug development in the past decade?
Gene and cell therapy products approved over the past decade in Europe and North America have provided new therapeutic options for single gene disorders and for hematologic malignancies. Lessons learned, and limitations identified, are reviewed.
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Nature Portfolio
2020
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oai:doaj.org-article:1f171a9d52474522a7b4c78c99203c642021-12-02T17:33:12ZTurning genes into medicines—what have we learned from gene therapy drug development in the past decade?10.1038/s41467-020-19507-02041-1723https://doaj.org/article/1f171a9d52474522a7b4c78c99203c642020-11-01T00:00:00Zhttps://doi.org/10.1038/s41467-020-19507-0https://doaj.org/toc/2041-1723Gene and cell therapy products approved over the past decade in Europe and North America have provided new therapeutic options for single gene disorders and for hematologic malignancies. Lessons learned, and limitations identified, are reviewed.Katherine A. HighNature PortfolioarticleScienceQENNature Communications, Vol 11, Iss 1, Pp 1-4 (2020) |
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DOAJ |
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DOAJ |
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EN |
| topic |
Science Q |
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Science Q Katherine A. High Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| description |
Gene and cell therapy products approved over the past decade in Europe and North America have provided new therapeutic options for single gene disorders and for hematologic malignancies. Lessons learned, and limitations identified, are reviewed. |
| format |
article |
| author |
Katherine A. High |
| author_facet |
Katherine A. High |
| author_sort |
Katherine A. High |
| title |
Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| title_short |
Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| title_full |
Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| title_fullStr |
Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| title_full_unstemmed |
Turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| title_sort |
turning genes into medicines—what have we learned from gene therapy drug development in the past decade? |
| publisher |
Nature Portfolio |
| publishDate |
2020 |
| url |
https://doaj.org/article/1f171a9d52474522a7b4c78c99203c64 |
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AT katherineahigh turninggenesintomedicineswhathavewelearnedfromgenetherapydrugdevelopmentinthepastdecade |
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