An Overview of the Clinical Characteristics of Japanese Patients with Spinal Muscular Atrophy: Data from SMART Consortium
Background: Patient registries play an important role in rare disease, particularly for recruitment of clinical trials and clinical research.Methods: In 2012, we launched a registry for the purpose of clarifying the clinical characteristics of spinal muscular atrophy (SMA) in Japan and with the goal...
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Auteurs principaux: | Tamaki Kato, Mari Urano, Mari Matsuo, Kayoko Saito |
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Format: | article |
Langue: | EN |
Publié: |
Society of Tokyo Women's Medical University
2021
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Accès en ligne: | https://doaj.org/article/2648c86ee2814deb80c5f89adf45531c |
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