Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing
Therapeutic genome engineering relies on the development of reliable, robust and versatile tools. Here the authors develop Cas9-Cas9 chimeras with high target site activity that generate predictable deletions.
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Nature Portfolio
2018
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oai:doaj.org-article:463e5b127556499185f48ce65924481b2021-12-02T15:34:43ZOrthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing10.1038/s41467-018-07310-x2041-1723https://doaj.org/article/463e5b127556499185f48ce65924481b2018-11-01T00:00:00Zhttps://doi.org/10.1038/s41467-018-07310-xhttps://doaj.org/toc/2041-1723Therapeutic genome engineering relies on the development of reliable, robust and versatile tools. Here the authors develop Cas9-Cas9 chimeras with high target site activity that generate predictable deletions.Mehmet Fatih BolukbasiPengpeng LiuKevin LukSamantha F. KwokAnkit GuptaNadia AmraniErik J. SontheimerLihua Julie ZhuScot A. WolfeNature PortfolioarticleScienceQENNature Communications, Vol 9, Iss 1, Pp 1-12 (2018) |
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Science Q Mehmet Fatih Bolukbasi Pengpeng Liu Kevin Luk Samantha F. Kwok Ankit Gupta Nadia Amrani Erik J. Sontheimer Lihua Julie Zhu Scot A. Wolfe Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
description |
Therapeutic genome engineering relies on the development of reliable, robust and versatile tools. Here the authors develop Cas9-Cas9 chimeras with high target site activity that generate predictable deletions. |
format |
article |
author |
Mehmet Fatih Bolukbasi Pengpeng Liu Kevin Luk Samantha F. Kwok Ankit Gupta Nadia Amrani Erik J. Sontheimer Lihua Julie Zhu Scot A. Wolfe |
author_facet |
Mehmet Fatih Bolukbasi Pengpeng Liu Kevin Luk Samantha F. Kwok Ankit Gupta Nadia Amrani Erik J. Sontheimer Lihua Julie Zhu Scot A. Wolfe |
author_sort |
Mehmet Fatih Bolukbasi |
title |
Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
title_short |
Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
title_full |
Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
title_fullStr |
Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
title_full_unstemmed |
Orthogonal Cas9–Cas9 chimeras provide a versatile platform for genome editing |
title_sort |
orthogonal cas9–cas9 chimeras provide a versatile platform for genome editing |
publisher |
Nature Portfolio |
publishDate |
2018 |
url |
https://doaj.org/article/463e5b127556499185f48ce65924481b |
work_keys_str_mv |
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