Estimated prevalence of Niemann–Pick type C disease in Quebec

Abstract Niemann–Pick type C (NP-C) disease is an autosomal recessive disease caused by variants in the NPC1 or NPC2 genes. It has a large range of symptoms depending on age of onset, thus making it difficult to diagnose. In adults, symptoms appear mainly in the form of psychiatric problems. The pre...

Description complète

Enregistré dans:
Détails bibliographiques
Auteurs principaux: Marjorie Labrecque, Lahoud Touma, Claude Bhérer, Antoine Duquette, Martine Tétreault
Format: article
Langue:EN
Publié: Nature Portfolio 2021
Sujets:
R
Q
Accès en ligne:https://doaj.org/article/7b7034c9c309436abaf075521380d279
Tags: Ajouter un tag
Pas de tags, Soyez le premier à ajouter un tag!