Economic evaluation of betibeglogene autotemcel (Beti-cel) gene addition therapy in transfusion-dependent β-thalassemia

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Economic evaluation of betibeglogene autotemcel (Beti-cel) gene addition therapy in transfusion-dependent β-thalassemia

Background Standard of care (SoC) for transfusion-dependent β-thalassemia (TDT) requires lifelong, regular blood transfusions as well as chelation to reduce iron accumulation. Objective This study investigates the cost-effectiveness of betibeglogene autotemcel (‘beti-cel’; LentiGlobin for β-thalasse...

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Auteurs principaux:	Anuraag R. Kansal, Odette S. Reifsnider, Sarah B. Brand, Neil Hawkins, Anna Coughlan, Shujun Li, Lael Cragin, Clark Paramore, Andrew C. Dietz, J. Jaime Caro
Format:	article
Langue:	EN
Publié:	Taylor & Francis Group 2021
Sujets:	beta-thalassemia economic evaluation gene therapy Public aspects of medicine RA1-1270 Business HF5001-6182
Accès en ligne:	https://doaj.org/article/d6cb861054544eae9f3fd0425864a1ec
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