Implications of circulating neurofilamentsfor spinal muscular atrophytreatment early in life: A case series

This longitudinal cohort study aimed to determine whether circulating neurofilaments (NFs) can monitor response to molecular therapies in newborns with spinal muscular atrophy (SMA; NCT02831296). We applied a mixed-effect model to examine differences in serum NF levels among healthy control infants...

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Détails bibliographiques
Auteurs principaux: Christiano R.R. Alves, Marco Petrillo, Rebecca Spellman, Reid Garner, Ren Zhang, Michael Kiefer, Sarah Simeone, Jihee Sohn, Eric J. Eichelberger, Emma Rodrigues, Elizabeth A. Arruda, Elise L. Townsend, Wildon Farwell, Kathryn J. Swoboda
Format: article
Langue:EN
Publié: Elsevier 2021
Sujets:
SMA
Accès en ligne:https://doaj.org/article/db25a4904c724193bfc8efc310be8954
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