Silencing Nfix rescues muscular dystrophy by delaying muscle regeneration

Strategies aimed at promoting muscle regeneration to treat muscular dystrophy have met with limited success. Here the authors show instead that delaying muscle regeneration, by ablation of the transcription factor Nfix, ameliorates muscular dystrophy in mice.

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Bibliographic Details
Main Authors: Giuliana Rossi, Chiara Bonfanti, Stefania Antonini, Mattia Bastoni, Stefania Monteverde, Anna Innocenzi, Marielle Saclier, Valentina Taglietti, Graziella Messina
Format: article
Language:EN
Published: Nature Portfolio 2017
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Online Access:https://doaj.org/article/4dfcc452d0b14567b01bb5bcd9666918
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Summary:Strategies aimed at promoting muscle regeneration to treat muscular dystrophy have met with limited success. Here the authors show instead that delaying muscle regeneration, by ablation of the transcription factor Nfix, ameliorates muscular dystrophy in mice.