Randomized and non-randomized designs for causal inference with longitudinal data in rare disorders
Abstract In the United States, approximately 7000 rare diseases affect 30 million patients, and only 10% of these diseases have existing therapies. Sound study design and causal inference methods are essential to demonstrate the therapeutic efficacy, safety, and effectiveness of new therapies. In th...
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| Auteurs principaux: | , |
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| Format: | article |
| Langue: | EN |
| Publié: |
BMC
2021
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| Accès en ligne: | https://doaj.org/article/9253ab0790f24de99be7790223c1c8ff |
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